Follow RSS for latest reports on this topicOrphan Drugs - Market Research and Reports

An orphan drug is a pharmaceutical product aimed at rare diseases or disorders. The development of orphan drugs has been financially incentivised through US law via the ‘Orphan Drug Act of 1983’. The National Organization for Rare Disorders (NORD), which was instrumental in establishing the 1983 Act, currently estimates 30 million Americans suffer from 7,000 rare diseases. Prior to the 1983 Act, 38 orphan drugs were approved. To date, 425 indication designations covering 347 drugs have been approved.

The success of the original Orphan Drug Act in the US led to it being adopted in other key markets, most notably in Japan in 1993 and the European Union in 2000.

Rare Disease Patient Populations are Defined in Law as:

  • USA: <200,000 patients (<6.37 in 10,000, based on US population of 314m)
  • EU: <5 in 10,000 (<250,000 patients, based on EU population of 506m)
  • Japan: <50,000 patients (<4 in 10,000 based on Japan population of 128m)

BioPortfolio's Easy Ordering System

  1. Search for the report you need from our store
  2. Make online payment with our easy checkout process
  3. Receive PDF report via email

Easy Online Payment or Pro Forma Invoice

We accept the following credit cards...



or can supply a pro-forma invoice if required.

Related Reports:

We found over 40 reports that matched your search.

Next 40 Matches >

Refine your search, and find more matches, using the form above.

Published:
2018-07-10

Published by: Global Markets Direct

Prices Starting From:
$3500

Published:
2017-08-29

Published by: Global Markets Direct

Prices Starting From:
$3500

Pharmaceutical Drugs Market Global Report 2017 Including: Cardiovascular Drugs, Dermatological Drugs, Gastrointestinal Drugs, Genito-Urinary Drugs, Hematology Drugs, Drugs For Infectious Diseases, Drugs For Metabolic Disorders, Drugs For Musculoskeletal Disorders, Central Nervous System Drugs, Oncology Drugs, Ophthalmology Drugs, Drugs For Respiratory Diseases Covering: Johnson & Johnson, Novarti [Report Updated: 17-07-2017]

The market segments in the pharmaceuticals drugs sector as of 2016 were Oncology, Anti-diabetics, Anti-rheumatics, Anti-virals, Vaccines, Bronchodilators, Sensory Organs, Anti-hypertensives, MS Therapies, Immunosuppressants, Anti-coagulants, Dermatologicals, Anti-hyperlipidaemics, Anti-fibrinolytics and Anti-bacterials.


Pharmaceuticals Drugs was the largest segment in the pharmaceuticals market with over 80% share of tRead More >>>

Published:
2017-07-17

Published by: The Business Research Company

Prices Starting From:
$6000

Cardiovascular Drugs Market Global Report 2017 Including: Anti-Hypertensive Drugs, Hypolipidemics, Anti Thrombotics, Other Drugs For Cardiovascular Diseases (Congestive Heart Failure, Anti-Arrythmic And Anti-Anginal Drugs) Covering: Bristol-Myers Squibb Company, Abbott Laboratories Inc., AstraZeneca PLC, Bayer AG, and Novartis AG [Report Updated: 17-07-2017]

Cardiovascular disorders drug market covers the drugs used to treat conditions that affect heart or blood vessels. These conditions include heart stroke, coronary artery diseases, valvular diseases, peripheral venous diseases, pericarditis, endocarditis, cardiac tumors, arteriosclerosis, and lymphatic diseases. Some of the major cardiovascular drugs include anticoagulants such as Rivaroxaban (Xarelto), Dabigatran (Pradaxa), Apixaban (Eliquis),Read More >>>

Published:
2017-07-17

Published by: The Business Research Company

Prices Starting From:
$4000

Published:
2017-07-17

Published by: The Business Research Company

Prices Starting From:
$4000

Genito-Urinary Drugs Market Global Report 2017 Including: Hormonal Contraceptives, Drugs For Benign Prostatic Hypertrophy, Drugs For Infertility, Drugs For Erectile Dysfunction, Drugs For Urinary Incontinence And Overactive Bladder, Drugs For Infections And Others, Drugs For Harmonal Replacement Therapy, Diuretics Covering: Pfizer Inc., Bristol-Myers Squibb Company, F. Hoffmann-La Roche Ltd, Abb [Report Updated: 17-07-2017]

The genitourinary drugs market covers drugs that are used in the treatment of diseases such as urinary tract infections, male reproductive diseases, voiding diseases, female reproductive diseases, glomerular disorders, urinary calculi, cystic kidney disease, Reno vascular diseases, benign prostate diseases, and other related diseases.


Some of the major drugs in the market include Avastin, Trimethoprim/sulfamethoxazolRead More >>>

Published:
2017-07-17

Published by: The Business Research Company

Prices Starting From:
$4000

Published:
2017-07-17

Published by: The Business Research Company

Prices Starting From:
$4000

Global Orphan Drugs Market by Disease Type (Oncologic Diseases, Metabolic Diseases, Hematologic and Immunologic Diseases, Infectious Diseases, Neurologic Diseases and Other Rare Diseases), Indication (Non-Hodgkin Lymphoma, Acute Myeloid Leukemia, Cystic Fibrosis, Glioma, Pancreatic Cancer, Ovarian Cancer, Multiple Myeloma, Duchenne Muscular Dystrophy, Graft vs Host Disease, Renal Cell Carcinoma an [Report Updated: 24-04-2017]

The pharmaceutical agents that are administered to treat, diagnose, and prevent life-threatening diseases (rare diseases) are known as orphan drugs. The global orphan drugs market accounted for 6 billion in 2015, and is anticipated to reach 9 billion by 2022, registering a CAGR of 6.8% from 2016 to 2022.nnOrphan drugs are used to treat rare (orphaned) diseases prevalent in a very small patie...Read More >>>

Published:
2017-04-24

Published by: Allied Market Research

Prices Starting From:
$5370

Published:
2016-11-01

Published by: Current Partnering

Prices Starting From:
$1495

Systemic Lupus Erythematosus Market: By Therapies (Antimalarial Drugs, Non-Steroidal Anti-Inflammatory Drugs (Nsaids), Corticosteroids Cytotoxic & Immunosuppressive Drugs, Biologics, Small Molecules) & By Region (Asia-Pacific, Others)-Forecast (2016-2021) [Report Updated: 22-09-2016]

Systemic lupus erythematosus, also commonly known as lupus, is an autoimmune disease which results in inflammation of tissues in the body with common symptoms like fever, fatigue, skin rashes, malaise, joint pain, and temporary loss of cognitive ability. Immune response is directed toward the body’s own cells, resulting in acute or chronic inflammation. Symptoms of lupus are general and hence of...Read More >>>

Published:
2016-09-22

Published by: Industry ARC

Prices Starting From:
$5250

Branded Generics Market: By Type (Value Added and Trade Named); By Applications: (Cardiovascular Drugs, Anti-Cancer Drugs, CNS Drugs, Anti-Infective Drugs); By Distribution (Retail Pharmacies, Hospital Pharmacies and Clinics); By Geography & Forecast – (2016 -2021) [Report Updated: 23-02-2016]

Branded generics drugs are similar to the innovator products but are marketed and sold under different brand names. The color, size and shape of the brands of the same medicine may vary depending on the manufacturing company. Branded generics cover a broad range of treatments including antibiotics, antifungal medications and diabetic therapies among many others. Global market for branded generics ...Read More >>>

Published:
2016-02-23

Published by: Industry ARC

Prices Starting From:
$5250

Published:
2016-02-09

Published by: Industry ARC

Prices Starting From:
$5250

Additional Searches

You may also like to search separately for: Orphan Drugs

We Stock...

{STICKYFOOTERMOBILE}